Oral Presentation ASPCR-ASDR Conference 2013

Induction of endoplasmic reticulum stress as a strategy for melanoma therapy (#47)

Nikolas K Haass 1 2 3 , David S Hill 1 , Kimberley A Beaumont 1 , Andrea Anfosso 1 , Penny E Lovat 4 , Wolfgang Weninger 1 2 5
  1. The Centenary Institute, Newtown, Australia
  2. Discipline of Dermatology, University of Sydney, Sydney, NSW, Australia
  3. University of Queensland, The University of Queensland Diamantina Institute, Translational Research Institute , Woolloongabba, Australia
  4. Newcastle University, Dermatological Sciences, Newcastle, Australia
  5. Department of Dermatology, Royal Prince Alfred Hospital, Camperdown, NSW, Australia

We have shown in vitro and in vivo, that melanomas are composed of differentially cycling tumour cells in a subcompartment-specific distribution, which may result in differential sensitivity to apoptosis. Further, we have demonstrated that targeting the endoplasmic reticulum (ER) with fenretinide (synthetic retinoid) or bortezomib (26S proteasome inhibitor) induces cell cycle arrest and apoptosis of metastatic melanoma cells in vitro and in vivo. This study aims (1) to investigate the effect of ER
stress-inducing drugs on the dynamics of cell division and cell death of individual melanoma cells within the complex tumour microenvironment, and (2) to develop combination strategies that increase the efficacy of ER stress-inducing agents for the treatment of melanoma.
We made use of the fluorescent ubiquitination-based cell cycle indicator (FUCCI), which facilitates the identification of individual proliferating cells in G1 versus S/G2/M cell cycle phases, in combination with confocal and multiphoton microscopy to track melanoma cell proliferation in realtime. We utilised the F-XBP1ΔDBD-venus reporter construct, which labels the cytoplasm of cells in response to ER stress.
We show that bortezomib induced ER stress, delayed cell cycle progression, and combination with fenretinide increased cell death in our 3D melanoma model. While the selective BRAF-inhibitor vemurafenib induced G1 arrest, bortezomib induced G1and G2 arrest, but preferentially killed G2-phase cells. Temozolomide enhanced the effect of bortezomib. However, MEK inhibitors blocked the effect of bortezomib in all melanoma cells, as did BRAF-inhibitors in BRAF mutant cells.
Our data suggest that bortezomib combined with fenretinide or temozolamide is a therapeutic strategy worth exploring for the treatment of BRAF-inhibitor insensitive or resistant melanoma. Importantly, melanoma cells in G1 are protected from the cytotoxic effect of bortezomib, which excludes MEK or BRAF inhibitors as combination partners.